Tokyo, July 1 -- UMIN Clinical Trials Registry (UMIN-CTR) received information related to the study (UMIN000061433) titled 'A retrospective observational study of the natural history and the effects of early diagnosis and treatment of pediatric neurological disorders' on July 1.
Study Type:
Observational
Primary Sponsor:
Institute - University of the Ryukyus
Condition:
Condition - Pediatric neurological diseases
Classification by malignancy - Others
Genomic information - NO
Objective:
Narrative objectives1 - This retrospective study will investigate differences in clinical presentation, treatment response, and long-term prognosis among children diagnosed with pediatric neurological disorders at our hospital, including cases diagnosed after the onset of symptoms and cases diagnosed before symptoms appeared. The aim is to examine factors influencing disease prognosis and contribute to the development of better medical care systems and guidelines for the future.
Basic objectives2 - Efficacy
Eligibility:
Age-lower limit - Not applicable
Age-upper limit - Not applicable
Gender - Male and Female
Key inclusion criteria - Patients diagnosed with pediatric neurological disorders who are receiving treatment at our hospital:
Target diseases: Spinal muscular atrophy, spinocerebellar degeneration, myasthenia gravis, muscular dystrophy, congenital myopathy, epilepsy, tuberous sclerosis, acute encephalitis/encephalopathy, hypoxic-ischemic encephalopathy, neurodevelopmental disorders, mitochondrial diseases, congenital metabolic disorders, hereditary dystonia, chromosomal abnormalities, fragile X syndrome, congenital malformation syndromes, neurodevelopmental disorders, chronic fatigue syndrome, orthostatic dysregulation, Long COVID, etc.
Key exclusion criteria - Not applicable
Target Size - 50
Recruitment Status:
Recruitment status - Preinitiation
Date of protocol fixation - 2026 Year 07 Month 01 Day
Anticipated trial start date - 2026 Year 07 Month 01 Day
Last follow-up date - 2030 Year 09 Month 30 Day
To know more, visit https://center6.umin.ac.jp/cgi-open-bin/ctr_e/ctr_view.cgi?recptno=R000070292
Disclaimer: Curated by HT Syndication.